pediatric Thalassemia Major
Showing 1 - 25 of >10,000
QoL of Pediatric Patients After HSCT and Its Influencing Factors
Not yet recruiting
- Thalassemia Major
- Acute Leukemia
- Conventional nursing
-
Guangzhou, Guangdong, ChinaSun Yat-sen Memorial Hospital, Sun Yat-sen University
Sep 4, 2023
Leukemia, Myeloid, Acute, Leukemia, B-cell, Leukemia, T Cell Trial in Monza (Sport Therapy)
Recruiting
- Leukemia, Myeloid, Acute
- +7 more
- Sport Therapy
-
Monza, MB, ItalyMaria Letizia Verga Center, Pediatric Clinic, University of Mila
Oct 24, 2022
Sickle Cell Anemia, Beta-thalassemia Major, Diamond-blackfan Anemia Trial in Pittsburgh (CD3/CD19 depleted leukocytes, CD45RA
Recruiting
- Sickle Cell Anemia
- +2 more
- CD3/CD19 depleted leukocytes
- +6 more
-
Pittsburgh, PennsylvaniaChildren's Hospital of Pittsburgh of UPMC
May 4, 2022
Bone Denisty Change in Children With Beta Thalassemia Major
Not yet recruiting
- Evaluate Bone Denisty Changes in Children With Beta Thalassemia Major
- Dexa scan
- (no location specified)
Sep 29, 2023
Iron Overload, Oxidative Stress, Thalassemia Major Trial in Bani Suwayf, Mecca (Omega 3, Nigella Sativa Oil, Hydroxyurea)
Completed
- Iron Overload
- +2 more
- Omega 3
- +5 more
-
Banī Suwayf, Egypt
- +3 more
Jan 25, 2021
Beta-Thalassemia Trial (CS-101 injection)
Not yet recruiting
- Beta-Thalassemia
- CS-101 injection
- (no location specified)
Sep 27, 2023
ß-thalassemia Trial in Shenzhen (ß-globin restored autologous hematopoietic stem cells)
Recruiting
- β-thalassemia
- β-globin restored autologous hematopoietic stem cells
-
Shenzhen, Guangdong, ChinaShenzhen Children's Hospital
Feb 24, 2023
Alpha Thalassemia Major, Hemoglobinopathy; With Thalassemia, Hemoglobinopathies Trial in San Francisco (in utero hematopoietic
Enrolling by invitation
- Alpha Thalassemia Major
- +8 more
- in utero hematopoietic stem cell transplantation
-
San Francisco, CaliforniaUniversity of California
Oct 28, 2022
Cognitive Function and Quality of Life in Thalassemic Children
Not yet recruiting
- Thalassemia
- Pediatric Quality of Life Inventory (questionnaire) and The Stanford-Binet Intelligence Scale fifth edition
-
Sohag, EgyptSohag university Hospital
Sep 25, 2023
Thalassemia, Beta, Thalassemia Major Trial in Tianjin (VGB-Ex01)
Not yet recruiting
- Thalassemia, Beta
- Thalassemia Major
- VGB-Ex01
-
Tianjin, Tianjin, ChinaRegenerative Medicine Center
Sep 11, 2023
ß Thalassemia Major Trial in Shanghai (?-globin reactivated autologous hematopoietic stem cells)
Active, not recruiting
- β Thalassemia Major
- γ-globin reactivated autologous hematopoietic stem cells
-
Shanghai, Shanghai, ChinaShanghai Bioray Laboratories Inc.
Oct 9, 2022
Cognitive Function, Fatigue and Health Related Quality of Life
Recruiting
- Cognitive Change
- +3 more
-
Giza, EgyptAbo El-Rish Pediatric Hospital
Jul 20, 2022
"Iron Overload and Endocrinological Diseases"
Recruiting
- Iron Overload
- +4 more
-
Modena, ItalyUnit of Endocrinology of Azienza Ospedaliero-Universitaria di Mo
Nov 13, 2023
Beta Thalassemia Major Anemia, Iron Overload Trial in Cairo, Jakarta (Deferiprone oral solution, Placebo)
Completed
- Beta Thalassemia Major Anemia
- Iron Overload
- Deferiprone oral solution
- Placebo
-
Cairo, Egypt
- +3 more
Feb 9, 2021
Alpha-Thalassemia, Alpha Thalassemia Major, Alpha Thalassemia Minor Trial in San Francisco
Recruiting
- Alpha-Thalassemia
- +2 more
-
San Francisco, CaliforniaUniversity of California San Francisco
Oct 7, 2022
Thalassemia Major Trial in Shanghai (?-globin reactivated autologous hematopoietic stem cells)
Not yet recruiting
- Thalassemia Major
- γ-globin reactivated autologous hematopoietic stem cells
-
Shanghai, Shanghai, ChinaShanghai Bioray Laboratories Inc
Jul 1, 2022
Beta-Thalassemia, Thalassemia, Genetic Diseases, Inborn Trial in Nashville (CTX001)
Recruiting
- Beta-Thalassemia
- +4 more
- CTX001
-
Nashville, Tennessee
- +5 more
Feb 2, 2023
Congenital Heart Surgery in Pediatric Beta-Thalassemia Major
Completed
- Hemolysis
- Hemolysis
- (no location specified)
Apr 27, 2020
Pulmonary Hypertension (PAH) in Patients With Thalassemia
Completed
- Thalassemia Major
- +2 more
- Physician standard-of-care according to ESC/ERS Guidelines
-
Orbassano, Turin, Italy
- +7 more
Aug 3, 2022
Transfusion Dependent Beta Thalassemia, Hemoglobinopathies, Thalassemia Major Trial in Nashville (EDIT-301)
Recruiting
- Transfusion Dependent Beta Thalassemia
- +3 more
- EDIT-301
-
Oakland, California
- +3 more
Jan 3, 2023
Hemoglobinopathies, Thalassemia, Sickle Cell Disease Trial in Banha (Hemoglobinopathy Nursing Program)
Completed
- Hemoglobinopathies
- +3 more
- Hemoglobinopathy Nursing Program
-
Banhā, Other, EgyptBenha University
May 21, 2022
Thalassemia Major, Transfusion-dependent Anemia Trial in Guangzhou (Luspatercept Injectable Product)
Recruiting
- Thalassemia Major
- Transfusion-dependent Anemia
- Luspatercept Injectable Product
-
Guangzhou, Guangdong, ChinaThe second affiliated hospital of Sun Yat-sen University
Jul 15, 2022
Sickle Cell Disease, Thalassemia Major Trial in Philadelphia (CliniMACS)
Recruiting
- Sickle Cell Disease
- Thalassemia Major
- CliniMACS
-
Philadelphia, PennsylvaniaChildren's Hospital of Philadelphia
Dec 22, 2021