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pediatric Thalassemia Major

Showing 1 - 25 of >10,000

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QoL of Pediatric Patients After HSCT and Its Influencing Factors

Not yet recruiting
  • Thalassemia Major
  • Acute Leukemia
  • Conventional nursing
  • Guangzhou, Guangdong, China
    Sun Yat-sen Memorial Hospital, Sun Yat-sen University
Sep 4, 2023

Leukemia, Myeloid, Acute, Leukemia, B-cell, Leukemia, T Cell Trial in Monza (Sport Therapy)

Recruiting
  • Leukemia, Myeloid, Acute
  • +7 more
  • Sport Therapy
  • Monza, MB, Italy
    Maria Letizia Verga Center, Pediatric Clinic, University of Mila
Oct 24, 2022

Sickle Cell Anemia, Beta-thalassemia Major, Diamond-blackfan Anemia Trial in Pittsburgh (CD3/CD19 depleted leukocytes, CD45RA

Recruiting
  • Sickle Cell Anemia
  • +2 more
  • CD3/CD19 depleted leukocytes
  • +6 more
  • Pittsburgh, Pennsylvania
    Children's Hospital of Pittsburgh of UPMC
May 4, 2022

Bone Denisty Change in Children With Beta Thalassemia Major

Not yet recruiting
  • Evaluate Bone Denisty Changes in Children With Beta Thalassemia Major
  • Dexa scan
  • (no location specified)
Sep 29, 2023

Iron Overload, Oxidative Stress, Thalassemia Major Trial in Bani Suwayf, Mecca (Omega 3, Nigella Sativa Oil, Hydroxyurea)

Completed
  • Iron Overload
  • +2 more
  • Omega 3
  • +5 more
  • Banī Suwayf, Egypt
  • +3 more
Jan 25, 2021

Beta-Thalassemia Trial (CS-101 injection)

Not yet recruiting
  • Beta-Thalassemia
  • CS-101 injection
  • (no location specified)
Sep 27, 2023

Thalassemia Major Trial (n-acetylcystine)

Not yet recruiting
  • Thalassemia Major
  • (no location specified)
Mar 9, 2023

ß-thalassemia Trial in Shenzhen (ß-globin restored autologous hematopoietic stem cells)

Recruiting
  • β-thalassemia
  • β-globin restored autologous hematopoietic stem cells
  • Shenzhen, Guangdong, China
    Shenzhen Children's Hospital
Feb 24, 2023

Alpha Thalassemia Major, Hemoglobinopathy; With Thalassemia, Hemoglobinopathies Trial in San Francisco (in utero hematopoietic

Enrolling by invitation
  • Alpha Thalassemia Major
  • +8 more
  • in utero hematopoietic stem cell transplantation
  • San Francisco, California
    University of California
Oct 28, 2022

Cognitive Function and Quality of Life in Thalassemic Children

Not yet recruiting
  • Thalassemia
  • Pediatric Quality of Life Inventory (questionnaire) and The Stanford-Binet Intelligence Scale fifth edition
  • Sohag, Egypt
    Sohag university Hospital
Sep 25, 2023

Thalassemia, Beta, Thalassemia Major Trial in Tianjin (VGB-Ex01)

Not yet recruiting
  • Thalassemia, Beta
  • Thalassemia Major
  • VGB-Ex01
  • Tianjin, Tianjin, China
    Regenerative Medicine Center
Sep 11, 2023

ß Thalassemia Major Trial in Shanghai (?-globin reactivated autologous hematopoietic stem cells)

Active, not recruiting
  • β Thalassemia Major
  • γ-globin reactivated autologous hematopoietic stem cells
  • Shanghai, Shanghai, China
    Shanghai Bioray Laboratories Inc.
Oct 9, 2022

Cognitive Function, Fatigue and Health Related Quality of Life

Recruiting
  • Cognitive Change
  • +3 more
    • Giza, Egypt
      Abo El-Rish Pediatric Hospital
    Jul 20, 2022

    "Iron Overload and Endocrinological Diseases"

    Recruiting
    • Iron Overload
    • +4 more
      • Modena, Italy
        Unit of Endocrinology of Azienza Ospedaliero-Universitaria di Mo
      Nov 13, 2023

      Beta Thalassemia Major Anemia, Iron Overload Trial in Cairo, Jakarta (Deferiprone oral solution, Placebo)

      Completed
      • Beta Thalassemia Major Anemia
      • Iron Overload
      • Deferiprone oral solution
      • Placebo
      • Cairo, Egypt
      • +3 more
      Feb 9, 2021

      Alpha-Thalassemia, Alpha Thalassemia Major, Alpha Thalassemia Minor Trial in San Francisco

      Recruiting
      • Alpha-Thalassemia
      • +2 more
        • San Francisco, California
          University of California San Francisco
        Oct 7, 2022

        Thalassemia Major Trial in Shanghai (?-globin reactivated autologous hematopoietic stem cells)

        Not yet recruiting
        • Thalassemia Major
        • γ-globin reactivated autologous hematopoietic stem cells
        • Shanghai, Shanghai, China
          Shanghai Bioray Laboratories Inc
        Jul 1, 2022

        Beta Thalassemia Major Anemia Trial (SP-420)

        Not yet recruiting
        • Beta Thalassemia Major Anemia
        • (no location specified)
        Jan 20, 2023

        Beta-Thalassemia, Thalassemia, Genetic Diseases, Inborn Trial in Nashville (CTX001)

        Recruiting
        • Beta-Thalassemia
        • +4 more
        • CTX001
        • Nashville, Tennessee
        • +5 more
        Feb 2, 2023

        Congenital Heart Surgery in Pediatric Beta-Thalassemia Major

        Completed
        • Hemolysis
        • Hemolysis
        • (no location specified)
        Apr 27, 2020

        Pulmonary Hypertension (PAH) in Patients With Thalassemia

        Completed
        • Thalassemia Major
        • +2 more
        • Physician standard-of-care according to ESC/ERS Guidelines
        • Orbassano, Turin, Italy
        • +7 more
        Aug 3, 2022

        Transfusion Dependent Beta Thalassemia, Hemoglobinopathies, Thalassemia Major Trial in Nashville (EDIT-301)

        Recruiting
        • Transfusion Dependent Beta Thalassemia
        • +3 more
        • EDIT-301
        • Oakland, California
        • +3 more
        Jan 3, 2023

        Hemoglobinopathies, Thalassemia, Sickle Cell Disease Trial in Banha (Hemoglobinopathy Nursing Program)

        Completed
        • Hemoglobinopathies
        • +3 more
        • Hemoglobinopathy Nursing Program
        • Banhā, Other, Egypt
          Benha University
        May 21, 2022

        Thalassemia Major, Transfusion-dependent Anemia Trial in Guangzhou (Luspatercept Injectable Product)

        Recruiting
        • Thalassemia Major
        • Transfusion-dependent Anemia
        • Luspatercept Injectable Product
        • Guangzhou, Guangdong, China
          The second affiliated hospital of Sun Yat-sen University
        Jul 15, 2022

        Sickle Cell Disease, Thalassemia Major Trial in Philadelphia (CliniMACS)

        Recruiting
        • Sickle Cell Disease
        • Thalassemia Major
        • CliniMACS
        • Philadelphia, Pennsylvania
          Children's Hospital of Philadelphia
        Dec 22, 2021